Earlier this year, researchers at Children's Hospital of Philadelphia and Penn created a first-of-its-kind drug customized to a unique genetic mutation to save an infant named Baby KJ from dying of a ...

Numerous natural products produced by microorganisms can be utilized as active ingredients to treat illnesses like cancer and infections. Although the microbes' genes contain the blueprints for these ...

Discover how scientists are harnessing the power of CRISPR to precisely edit DNA, revolutionizing medicine and ethics as they rewrite the very code of life. Pixabay, PublicDomainPictures CRISPR ...

A single infusion of an experimental gene-editing drug appears safe and effective for cutting cholesterol, possibly for life, according to a small early study released Saturday. The study, which ...

A new gene-editing technique enables the correction of multiple genetic mutations simultaneously, transforming the prospects for millions living with complex inherited diseases, such as cystic ...

Angiopoietin-like protein 3 (ANGPTL3) inhibits lipoprotein and endothelial lipases. ANGPTL3 loss-of-function genetic variants are associated with decreased levels of low-density lipoprotein ...

Entrepreneurs say it’s time to safety-test designer baby technology. A West Coast biotech entrepreneur says he’s secured $30 million to form a public-benefit company to study how to safely create ...

This is today's edition of The Download, our weekday newsletter that provides a daily dose of what's going on in the world of technology. Here’s the latest company planning for gene-edited babies The ...

"This technology could be important for in vivo delivery," meaning the delivery of gene editors directly into the body, said Gasiūnas, who is also chief scientific officer of the biotech company ...