ORLANDO -- A gene therapy that could transform CAR T-cell treatment achieved rapid and potentially durable measurable ...

He was cast as a real-life Dr Frankenstein, a scientist whose ego had led him to tamper with human life. After more than a ...

There is no cure for the rare disease Hereditary Spastic Paraplegia (HSP), but researchers from Drexel University’s College ...

There is no cure for the rare disease Hereditary Spastic Paraplegia (HSP), but researchers from Drexel University's College ...

ROME, Italy, Dec. 10, 2025 /PRNewswire/ -- Fondazione Telethon announced today that the U.S. Food and Drug Administration (FDA) has approved the Biologics License Application (BLA) for Waskyra, an ex ...

Fondazione Telethon announced today that the U.S. Food and Drug Administration (FDA) has approved the Biologics License Application (BLA) ...

Investment from XGEN Venture, British Business Bank, and a global biopharmaceutical company will support first-in-human Phase ...

Today, after receiving a gene therapy developed at the University of California San Diego, Natalie is thriving at 34 years ...

Texas Sen. John Cornyn sounded the alarm that a biotech startup firm that has raised some $30 million to study diseases in ...

Scientists at UCL and GOSH have used groundbreaking base-edited CAR‑T cell therapy — BE‑CAR7 — to treat aggressive T‑cell ...

A new wave of gene therapy treatments offer a new lease on life for people with inherited diseases such as haemophilia. But ...

MRD-negative response rate in four patients; all remain in response through the longest follow up of 5 monthsFavorable ...