ORLANDO -- A gene therapy that could transform CAR T-cell treatment achieved rapid and potentially durable measurable ...

On a video call in early September, Sarah Tabrizi first saw the data that she and other researchers studying Huntington’s ...

JABSOM Cell and Molecular Biology researcher Dr. Jesse Owens has spent the better part of two decades chasing a vision that ...

An 8-year-old boy made medical history thanks to Columbus doctors. Yet the city where it happened barely registered. Time we ...

THE INFORMATION CONTAINED WITHIN THIS ANNOUNCEMENT IS DEEMED BY THE COMPANY TO CONSTITUTE INSIDE INFORMATION AS STIPULATED UNDER THE MARKET ABUSE REGULATION (EU) NO. 596/2014 AS IT FORMS PART OF UK ...

ROME, Italy, Dec. 10, 2025 /PRNewswire/ -- Fondazione Telethon announced today that the U.S. Food and Drug Administration (FDA) has approved the Biologics License Application (BLA) for Waskyra, an ex ...

If approved, gene therapies could fill gaps in patient care left by CFTR modulators, notes GD Healthcare analyst, Vinie Varkey.

Ajinomoto launches CELLiST AAV Production Supplement 1, boosting gene therapy viral vector productivity by 1.3-2x.

Zevaskyn, the first gene therapy for recessive dystrophic epidermolysis bullosa, showed significant wound healing in phase 3 ...

Texas Sen. John Cornyn sounded the alarm that a biotech startup firm that has raised some $30 million to study diseases in ...

Qalsody is one step closer to being covered by public Canadian healthcare systems when used to treat adults with ALS with ...

A cutting-edge therapy using base-edited immune cells is offering a major breakthrough for patients with one of the toughest ...