In humans, only two genes have been reliably linked to gut bacteria: the lactase gene, which influences milk-digesting ...

Findings from two clinical trials suggest Novartis' Itvisma is safe and effective for SMA patients over two years old.

Backed by a handful of prominent investors including the Gates Foundation, the startup is pursuing an approach it believes ...

Researchers have developed a new "color-coded" genetic method that makes it easy to distinguish male and female mosquitoes.

CAR T-cell therapy can be a lifesaving treatment for blood cancers like leukemia and lymphoma. The gene therapy trains a patient’s T cells—white blood cells that play an important role in the immune ...

Researchers at the Icahn School of Medicine at Mount Sinai have developed a first-of-its-kind mRNA system that switches on therapeutic genes preferentially inside targeted cells—an advance ...

We're living in a moment where science fiction is becoming medical reality. Imagine a world where doctors can simply rewrite ...

A mom was overjoyed when she learned a gene therapy treatment could save her child's life, until she found out no one would cover the $2 million price tag.

Ajinomoto launches CELLiST AAV Production Supplement 1, boosting gene therapy viral vector productivity by 1.3-2x.

TN-401 was Well Tolerated at 3E13 vg/kg dose Robust Transduction and Demonstrated Increases in PKP2 Protein Levels in First Two Patients at Week ...

Although the readout was only from four multiple myeloma patients, attendees at the meeting wondered at how far the CAR T-cell therapy field has come.

Researchers at the University of Geneva, together with colleagues in Switzerland, France, the United States and Israel, ...